Trump fingers Robert F. Kennedy Jr. to lead the HHS, lupus and ATTR-CM dominate headlines this week, bluebird bio has a cash gap to leap and RegenxBio eyes Sarepta in Duchenne muscular dystrophy.
a potential best-in-class gene therapy for Duchennemusculardystrophy, has advanced to pivotal stage and dosed its first patient. The company also announced new, positive efficacy and safety ...