Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne, commemorated its 30th ...
Capricor Therapeutics (NASDAQ:CAPR) announced Wednesday that the European Medicines Agency has issued Orphan Drug and ...
Regenxbio is pushing its Duchenne muscular dystrophy gene therapy into pivotal development, with a BLA planned for ...
Milestone represents a significant step forward in the development of deramiocel for the treatment of Duchenne muscular ...
Throughout 2024, the FDA issued new drug approvals and expanded treatment indications across various rheumatologic diseases.
Regenxbio’s investigational gene therapy improved muscle function for patients with Duchenne muscular dystrophy (DMD) in a phase 1/2 study. | Regenxbio’s investigational gene therapy improved muscle ...
a potential best-in-class gene therapy for Duchenne muscular dystrophy, has advanced to pivotal stage and dosed its first patient. The company also announced new, positive efficacy and safety ...
It’s easy for those who play or watch the best movies based on video games to want to be immersed in that fictional world.
Elevidys, a gene therapy from Sarepta Therapeutics (SRPT.O), opens new tab approved in the United States last year for ...
Analyst Gena Wang from Barclays maintained a Buy rating on RegenXBio (RGNX – Research Report) and keeping the price target at $50.00.Don't Miss ...
Columnist Shalom Lim tells an international conference about his experiences with inclusion during his education in Singapore ...