Two Austin sisters are hopeful after the FDA recently approved two new treatments for their rare genetic disorder, ...
Zevra Therapeutics' drug, Miplyffa, for treating a rare and fatal genetic disorder will have a wholesale acquisition cost ...
A team of researchers from the Chinese Academy of Sciences has uncovered compelling evidence of a genetic link between ...
The play is known as the Jackson Special. Kelly Maynard, Jackson’s mom, said he was diagnosed with Duchenne’s Muscular ...
The U.S. Food and Drug Administration approved IntraBio's drug for a rare and fatal genetic disorder, the health regulator ...
After a seven-year search for answers, a family from Eden, Utah, has received a life-changing diagnosis for their daughter ...
Author: Dr Shrikant Jamdade, Clinical Geneticist, Mumbai Spinal Muscular Atrophy (SMA) is a common genetic disorder affecting ...
An Overland Park teen completed a 150-mile bike journey Sunday to raise awareness and hope for his rare genetic disorder.
Shares of Biohaven climbed 13% premarket on Monday after the biotech company said its treatment for a rare neurological ...