Mass General Brigham and Saudi healthcare leaders collaborate to redefine the future of healthcare through AI, gene therapy, ...

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

According to estimates by the World Federation of Hemophilia, nearly 80% of hemophilia cases in India remain undiagnosed, ...

CROs can contribute to site collaboration by also identifying and supporting non-academic institutions capable of conducting CGT trials. This includes identifying community-based researchers and ...

Genetic factors are thought to play a major role in the development of autism – but for decades what they are has proven elusive. Now scientists are starting to uncover clues.

At the GenScript Biotech Global Forum 2025, industry leaders celebrated CAR T cell therapy achievements while discussing ...

From STAT’s Matthew Herper: Pfizer said this morning that it would stop development of danuglipron, its experimental oral GLP-1 medicine to treat obesity, focusing its efforts on another medicine with ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

Hemophilia represents a rare, lifelong bleeding disorder characterized by the blood's inability to clot normally. While management strategies have advanced ...

A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.

Genflow Biosciences Signs MSA with Heureka Labs, Launching AI-Powered Partnership in Gene Therapy Research ...

Investigators have developed STITCHR, a new gene editing tool that can insert therapeutic genes into specific locations without causing unwanted mutations. The system can be formulated completely as ...