New guidelines for cystic fibrosis screening in newborns improve sensitivity, equity, and timeliness of diagnosis.

Vertex Pharmaceuticals today announced that the European Medicines Agency's (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for ALYFTREK® ...

Battling a rare mutation of cystic fibrosis, Emily Kramer-Golinkoff fights for her life — and for gene therapies that offer ...

Prescription charges in England will be frozen this year – for the first time since 2022.The charge for a single item will ...

Thanks to the little-known DWP rule, this means their payments could increase by £36.50, or by £146 a month from £295.60 to ...

Banning mRNA technology in response to the many missteps of public health officials during the pandemic is a textbook example ...

In the full study, conducted in collaboration with the Castiglione Lab at Vanderbilt University and partially funded by the ...

Baron Health Care Fund retreated in the first quarter of 2025, underperforming its benchmark, the Russell 3000 Health Care ...

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Leaders and advocates gather for the 9th Annual Leadership Summit of the Sickle Cell Community Consortium, celebrating ...

Medicines Discovery Catapult is driving national productivity in biotech and improving patients’ lives. Purposeful ...

Jonathan Rockoff is the Health Business editor at The Wall Street Journal, managing a team that reports on pharmaceutical and biotechnology companies, health insurers and hospitals. During the ...