SMA3h
Child doing well after mother had SMA treatment while pregnant
A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...
Neurology Advisor5h
FDA Approves Tablet Form of Evrysdi for Spinal Muscular Atrophy
The US Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for people living with spinal muscular atrophy (SMA).
pharmaphorum1d
SMA treatment with Evrysdi 'could start prenatally'
A pioneering team at St Jude Children's Research Hospital in the US say they successfully treated a child diagnosed with SMA ...
Barchart on MSN2d
2 Hot Growth Stocks Poised for Gains of Up to 370%, According to Wall Street
The biotech industry is ripe with great investment opportunities due to technological advancements such as artificial ...
Medpage Today on MSN2d
First-Ever Prenatal Treatment for Spinal Muscular Atrophy Shows Promise
The first prenatal therapy for spinal muscular atrophy (SMA) showed promising results, a case report indicated. More than 2 ...
Monthly Prescribing Reference3d
New Tablet Formulation of SMA Therapy Evrysdi Gets FDA Approval
The tablet formulation can either be swallowed whole or dispersed in a teaspoon of filtered (non-chlorinated) water.
Daily6d
USFDA Approves Roche's Evrysdi Tablet for Spinal Muscular Atrophy
Basel: Roche, announced that the U.S. Food and Drug Administration (FDA) has approved a New Drug Application (NDA) for an ...