Final book released in 'Raising a Hand' music photography series for Rett syndrome research
Photographers Kevin Black and Dave Clements have released the third of their three-volume "Raising A Hand" series that raises money for Rett syndrome research.
Parents Dismissed by Doctors After Noticing Newborn Daughter's Weakness. At 3, She's Diagnosed with Rare Disorder (Exclusive)
Two months after giving birth to their daughter, Jayla, Shelly Balboa and her partner, Joseph, noticed the left side of their ...
Promising Outlook for Neurogene’s Low-Dose NGN-401 Program in Rett Syndrome
Keith Tapper CFA, an analyst from BMO Capital, maintained the Buy rating on Neurogene (NGNE – Research Report). The associated price target ...
BioSpace21h
Neurogene Drops Batten Gene Therapy Program
Failing to receive the RMAT designation from the FDA for its early-stage Batten disease gene therapy, Neurogene tells ...
Inside Coleen Rooney's relationship with little sister Rosie: From caring for foster sibling during brain disorder battle to WAG's pilgrimages to pray for healing miracl…
The WAG, 38, spoke to her campmates about Rosie, who tragically passed away in 2013 aged 14 after a lifelong battle with Rett ...
Heart23h
Who is Coleen Rooney's sister Rosie McLoughlin?
Coleen Rooney has bravely opened up about the loss of her younger sister Rosie McLoughlin, leading many fans to want to know ...
FierceBiotech2d
Neurogene rethinks gene therapy trial after high dose leaves Rett patient in critical condition
Neurogene has dropped plans to keep studying the high dose of its Rett syndrome gene therapy because of an adverse event that ...
Coleen Rooney breaks down in tears as she opens up about family tragedy and bonds with fellow I'm A Celeb campmate Barry McGuigan over grief
Coleen Rooney was in tears as she opened up about the loss of her little sister Rosie during Monday's I'm A Celeb.
pharmaphorum1d
Neurogene falls again on Rett gene therapy side effects
In an update posted today, Neurogene said that the "emerging treatment-related serious adverse event (SAE)" was a case of systemic hyperinflammatory syndrome, a rare and life-threatening immune ...
FierceBiotech1d
Neurogene stops Batten gene therapy after FDA denies request
Talks with the FDA haven’t gone according to plan. Seeking a streamlined pathway, Neurogene submitted a Regenerative Medicine ...
Neurogene provides update on NGN-401 clinical trial for Rett syndrome
Neurogene (NGNE) announced an update on its ongoing Phase 1/2 open-label clinical trial evaluating NGN-401 gene therapy for the treatment of ...
BioSpace29m
RFK Jr.’s HHS Nomination, Biogen’s Lupus Win and Leqembi Struggles, Neurogene’s Rough Month, More
Trump fingers Robert F. Kennedy Jr. to lead the HHS, lupus and ATTR-CM dominate headlines this week, bluebird bio has a cash gap to leap and RegenxBio eyes Sarepta in Duchenne muscular dystrophy.