Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

Mass General Brigham and Saudi healthcare leaders collaborate to redefine the future of healthcare through AI, gene therapy, ...

A team at the Centro Nacional de Investigaciones Cardiovasculares (CNIC) has developed an innovative gene-therapy strategy ...

Discover how an emerging technology called tRNA therapy could become the next big thing in genetic disease treatment.

UMass Chan Medical School has laid off or furloughed 200 employees, as the campus grapples with cuts to NIH research and ...

Feb. 7, 2025 — A research team has made a major discovery on how the CUL5 gene affects CAR-T cell therapy, an advanced cancer therapy. The study reveals that reducing the activity of the CUL5 ...

Gene therapy is an area of intensive research and development in the retina space, with promising prospects and significant challenges. The benefits and pitfalls of gene therapy were discussed by two ...

Investigators have developed STITCHR, a new gene editing tool that can insert therapeutic genes into specific locations without causing unwanted mutations. The system can be formulated completely as ...