Researchers found that the local release of dopamine – a molecule best known for its role in the brain’s reward system – is a ...

If administered early, gene therapy has the potential to change the medical history of children born with metachromatic ...

THURSDAY, April 17, 2025 (HealthDay News) -- Children who spend more time playing outdoors or participating in different ...

SMA patients who can sit see improvements in motor function over 12 months of treatment with DMTs, particularly in fine motor ...

A case report in Japan shows Spinraza helped a boy with SMA type 0 sit without support for a short time at age 2 and stand ...