The drug has since collected additional nods in atypical hemolytic uremic syndrome (aHUS), generalized myasthenia gravis (gMG) and pediatric gMG, plus neuromyelitis optica spectrum disorder.

That covers all of the FDA-approved indications for Soliris (eculizumab), except for neuromyelitis optica spectrum disorder (NMOSD) which remains protected by use patents. The US launch of the two ...

Further Soliris projects remain central to its plans, and include eculizumab for Relapsing Neuromyelitis Optica Spectrum Disorder, with phase 3 data expected next year. It also has a next ...

Marla Black Morgan, MD, with Phoebe Neurology Associates, presented findings on a study into the diagnostic journey of patients with neuromuscular conditions who have rare diseases at the 2025 ...

With UPLIZNA receiving a label expansion that opens the door to a previously untapped rare disease market, Amgen is seeing strong returns on its USD 27.8 billion acquisition of Horizon ...

Is nitrogen fertilizer supercharging allergy-causing pollen? Nitrogen-fertilized grasslands may produce six times more pollen than their unfertilized counterparts, suggests a study published in ...

The findings are ... New Genetic Cause of Neurodevelopmental Disorders Apr. 10, 2025 — A seminal study has uncovered a new genetic cause of neurodevelopmental disorders (NDDs). The discovery ...

Mar. 11, 2025 — For people with a certain sleep disorder, a simple blood test could help predict the development of dementia years before symptoms appear, a new study indicates. Idiopathic REM ...

Autism spectrum disorders are a group of neurodevelopmental disorders that are characterized by impaired social interaction and communication skills, and are often accompanied by other behavioural ...