Pub manager Natalie Grenfell said: “I want to say a huge and heartfelt thank you to everyone who came along to our first ever ...

Vertex Pharmaceuticals today announced that the European Medicines Agency's (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for ALYFTREK® ...

Jonathan Rockoff is the Health Business editor at The Wall Street Journal, managing a team that reports on pharmaceutical and biotechnology companies, health insurers and hospitals. During the ...

Battling a rare mutation of cystic fibrosis, Emily Kramer-Golinkoff fights for her life — and for gene therapies that offer ...

People with diseases caused by rare mutations have fewer options and poorer prospects than other patients despite rapid ...