The US Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for people living with spinal muscular atrophy (SMA).
Live Science on MSN16h
Deadly motor-neuron disease treated in the womb in world 1stAn infant with a fatal genetic disease has survived past the age of 2 with no signs of the condition, thanks to treatment ...
A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...
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