Trump fingers Robert F. Kennedy Jr. to lead the HHS, lupus and ATTR-CM dominate headlines this week, bluebird bio has a cash gap to leap and RegenxBio eyes Sarepta in Duchenne muscular dystrophy.

Photographers Kevin Black and Dave Clements have released the third of their three-volume "Raising A Hand" series that raises money for Rett syndrome research.

Keith Tapper CFA, an analyst from BMO Capital, maintained the Buy rating on Neurogene (NGNE – Research Report). The associated price target ...

Failing to receive the RMAT designation from the FDA for its early-stage Batten disease gene therapy, Neurogene tells ...

The WAG, 38, spoke to her campmates about Rosie, who tragically passed away in 2013 aged 14 after a lifelong battle with Rett ...

Coleen Rooney has bravely opened up about the loss of her younger sister Rosie McLoughlin, leading many fans to want to know ...

Coleen Rooney's little sister Rosie died when she was just 14 and the I'm A Celeb star, who tried to stay strong for her ...

Talks with the FDA haven’t gone according to plan. Seeking a streamlined pathway, Neurogene submitted a Regenerative Medicine ...

Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and families affected by rare neurological diseases ...

Former professional boxer Barry McGuigan has opened about the death of his daughter, while appearing on I'm a Celebrity...

Coleen Rooney has broken down in tears as she opened up about a family tragedy on I'm A Celeb. The 38-year-old opened up ...

Coleen Rooney was in tears as she opened up about the loss of her little sister Rosie during Monday's I'm A Celeb.